Rescuing and Repurposing Drugs: Challenges and Opportunities

Track:
Rare/Orphan Diseases

Day & Time:
June 26, 4:00PM - 5:30PM

Session Number:
385

Room Number:
205B

Level:
Intermediate

Type:
Forum

Title:
Rescuing and Repurposing Drugs: Challenges and Opportunities

Chair(s):
Cindy Luxhoj Hahn
President and CEO
Alagille Syndrome Alliance, United States

Description:
Drug rescue and repurposing presents an opportunity to spur the drug development process by building upon previous research and development efforts. However, this strategy also has challenges, particularly related to treatments for rare/orphan diseases.

Learning Objective(s):
Discuss the value of NCATS' program in spurring the drug development process; Describe challenges inherent in drug rescue and repurposing; Identify the innovative partnering opportunities and potential for accelerated therapeutic discoveries presented by this strategy.

Presentation(s) & Speaker(s):
A Case Study
Ciara Kennedy, PhD,MBA,MSc
Vice President, Operations
Lumena Pharmaceuticals, United States

Regulatory Challenges of Rescue and Repurposing
Larissa Lapteva
Medical Officer, Rare Diseases Program, Office of New Drugs, CDER
FDA, United States

Catalyzing Innovation at the National Center for Advancing Translational Sciences
John C. McKew, PhD
Acting Director, Division of Preclinical Innovation
National Center for Advancing Translational Sciences, United States